Online Issues

<< All issues


Order online

ILAR Journal Volume 50(2)
Gene Therapy in Large Animal Models of Human Genetic Diseases

107 Introduction: Gene Therapy in Large Animal Models of Human Genetic Diseases
John H. Wolfe   | Link to Full Text
112 Gene Therapy for Lysosomal Storage Diseases (LSDs) in Large Animal Models
Mark Haskins   |
122 Gene Therapy for Inherited Metabolic Disorders in Companion Animals
Dwight D. Koeberl, Carlos Pinto, Talmage Brown, and Y.T. Chen   |
128 Large Animal Models of Neurological Disorders for Gene Therapy
Christine Gagliardi and Bruce A. Bunnell   |
144 Protein Replacement Therapy and Gene Transfer in Canine Models of Hemophilia A, Hemophilia B, von Willebrand Disease, and Factor VII Deficiency
Timothy C. Nichols, Aaron M. Dillow, Helen W.G. Franck, Elizabeth P. Merricks, Robin A. Raymer, Dwight A. Bellinger, Valder R. Arruda, and Katherine A. High   | |
168 Potential Large Animal Models for Gene Therapy of Human Genetic Diseases of Immune and Blood Cell Systems
Thomas R. Bauer Jr., Rima L. Adler, and Dennis D. Hickstein |
187 Gene Therapy in Large Animal Models of Muscular Dystrophy
Zejing Wang, Jeffrey S. Chamberlain, Stephen J. Tapscott, and Rainer Storb |
199 Gene Therapy in Large Animal Models of Human Cardiovascular Genetic Disease
Meg M. Sleeper, Lawrence T. Bish, and H. Lee Sweeney |
206 AAV-Mediated Gene Therapy for Retinal Disorders in Large Animal Models
Knut Stieger, Elsa Lhériteau, Philippe Moullier, and Fabienne Rolling |
225 Large Animal Models of Genetic Disease: Pertinent IACUC Issues
N. Matthew Ellinwood and Colin M. Clay |
229 Thanks to Institutional Supporters
230 ILAR Publications
235 ILAR Publications Order Form
237 ILAR Journal Subscription Order Form
239 ILAR Journal Individual Issues Order Form





Copyright © 2008. National Academy of Sciences.
All rights reserved.
500 Fifth St. N.W., Washington, D.C. 20001.
Terms of Use and Privacy Statement